Burst Expert Illustrations and Commentaries™: Visualizing Gene Therapy Approaches in Hemophilia A

Target Audience

This educational activity is directed toward hematologists, pediatricians, and primary care clinicians, medical geneticists, nurses, and other healthcare professionals who care for patients with hemophilia.

Activity Overview

This Burst Expert Illustrations and Commentaries™ is a video-based program in which an expert discusses the etiology and emerging treatment of hemophilia A. In this activity, the faculty focuses on the pathophysiology of hemophilia A relevant to the use of gene therapy, which is currently under investigation. This discussion is enriched with the use of video animation to illustrate the mechanism of disease.

Learning Objectives

Upon completion of this activity, participants should be better able to:

Assess the severity of hemophilia A according to clinical presentation and results of factor assays
Analyze the potential impact of emerging therapies on the management of hemophilia A