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EXCEL Continuing Education

A Platform for Gene Therapy Delivery: Adeno-Associated Virus (AAV) Vectors

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Overview / Abstract:

The goal of gene therapy is to treat diseases at the genetic level by replacing deficient enzymes in target tissues, therefore, changing the course of the disease. Simply stated, it is the transfer of genetic material for disease therapy or prevention. Gene therapy with adeno-associated virus (AAV) vectors has demonstrated safety and long-term efficacy in several trials across target organs, including eye, liver, skeletal muscle, and the central nervous system.

The goal of this CME-certified activity is to increase physicians' knowledge of clinical considerations relating to the use of adeno-associated virus (AAV) vectors in gene therapy, and its impact on the treatment of several rare disorders.

Expiration

Sep 08, 2022

Discipline(s)

Nurse Practitioner , Nursing CNE, Physician CME, Physician Assistant CME

Format

Webinar / Webcast / Video

Credits / Hours

.75

Accreditation

ACCME

Presenters / Authors / Faculty

Eric T. Rush, MD, FAAP, FACMG
Clinical Geneticist
Underdown/Yeomans Family Endowed Professor in Connective Tissue Disorders Care
Medical Director, Office of Faculty Development
Children’s Mercy Kansas City
Associate Professor of Pediatrics
University of Missouri – Kansas City School of Medicine
Clinical Associate Professor of Internal Medicine
University of Kansas School of Medicine

Activity Specialities / Related Topics

Genetics, Nephrology, Pathology, Pediatrics

Sponsors / Supporters / Grant Providers

Ultragenyx Pharmaceutical

Keywords / Search Terms

EXCEL Continuing Education Rare disorders, (please add hepatology to your specialty list), Adeno-Associated Virus, gene therapy. Free CE CME

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