Duchenne Muscular Dystrophy: Recognizing Its Earliest Signs in Infancy and Care Transition into Adulthood

Target Audience
The intended audience for this activity are neurologists, neuromuscular specialists, pediatric neurologists, genetic counselors, and pediatricians.

Program Overview
Join a panel of expert clinicians to identify the subtle and very early signs of DMD that may be detected before functional symptoms are noticed and that can help earlier diagnoses and appropriate interventions. Panelists will review the importance of matching mutations to therapeutic decisions, discuss emerging concepts around functional and non-functional outcomes of treatment success, and share strategies to optimize care related to mood, bone health, and transitions from pediatric to adult care.

Learning Objectives
Upon completion of this activity, participants should be better able to:

Summarize the early signs of muscle injury that often precede development of visible symptoms in DMD
Define how genetic testing can influence treatment decisions
Explain how early treatment with DMTs can alter the natural history of DMD
Examine functional and non-functional outcomes and how they influence the definition of treatment success
Identify components of multidisciplinary care for patients with DMD, including optimizing mood, bone health, and plans to transition from pediatric to adult care